Effector T cells Disease modifiers Chondrocytes MRNP assembly Albumin gene targeting Distal myopathy Disease heterogeneity Cell stemness Mouse model GABA Brain MRI Glucocorticosteroid Cofilin-1 Dilated cardiomyopathy Adenosine Biomarker Les paramètres respiratoires Brain damage AICD Spinal muscular atrophy Fabry disease lysosomal storage disorders adeno asociated virus-9 Amyotrophic Lateral Sclerosis Biological marker Brain Prematurity Biomarkers Epigenetic changes Gene therapy IPSCs Lentiviral vectors FOXO3a Adult SMA Cartilage and bone regeneration Dicer Longitudinal progression DPRs Aav10 Clinical markers Diseases Adult patients Cell reprogramming Bioinformatics GeneRide Bone involvement Maternal behavior Maternal malnutrition ASO Functional outcomes Brain imaging CRISPR/SaCas9 Maladie neuromusculaire Extremely preterm infants IRM G-Secretase Inflammation Amyotrophie spinale FTD Genetical therapy ASOs MUNIX Intra-uterine growth restriction C9orf72 Brain development Antisense oligonucleotides Brain injury Long-term handicap AAV Coagulation factor IX Gene transfer SMN CNS Blood brain barrier ERK1/2 signaling MRI Fetal growth restriction FGR 3xTgAD Mice Early-onset sepsis Neuromuscular disease Clinical trial Bone development IUGR Calcium handling Skeletal muscle ALS MiRNA Microglia Icv Errance diagnotique MND Mecp2 Melatonin Clinical trials Genetics DTI Cellules souches musculaires Intra-CSF delivery LMNA Duchenne Muscular Dystrophy Modèle murin